Scientists using gene therapy have partially restored hearing and balance in profoundly deaf mice, according to a study published on Monday in the journal Nature Medicine. The research, still in its early stages and restricted to lab animals, may open up new avenues for tackling Usher syndrome, an inherited form…
Dutch biotech company uniQure said Monday it would start selling the first human gene therapy to be approved in the West by mid-2013 and predicted an explosion of similar therapies to come. The European Commission approved Glybera on October 25, making the drug for treating the extremely rare disorder lipoprotein…
WASHINGTON — US scientists on Wednesday reported a new advance in using gene therapy to restore eyesight in people with a rare, inherited form of blindness. The therapy, which had been previously tried in just one eye of 12 people, worked well when injected into the other eye of three…